In this paper published by researchers in Japan, 3 Japanese female patients (47, 55 & 56-year-old) were diagnosed of Bietti’s Crystalline Dystrophy (BCD), a rare blinding disease.
In this paper published by researchers in Japan, 3 Japanese female patients (47, 55 & 56-year-old) were diagnosed of Bietti’s Crystalline Dystrophy (BCD), a rare blinding disease.
Richard Yang, Founder & CEO of ReflectionBio and a rare disease patient, was invited to join the newly formed “Orphan Drug Development Guidebook” Task Force of International Rare Diseases Research Consortium (IRDiRC).
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(October 2018) Richard Yang, Founder & CEO of ReflectionBio and a rare disease patient, was invited to join the newly formed “Orphan Drug Development Guidebook” Task Force of International Rare Diseases Research Consortium (IRDiRC). The “Orphan Drug Development Guidebook” project aims at creating a simple guidebook for academic and industrial drug developers describing the available tools and initiatives specific for rare disease development and how to best use them.
“I am proud to be working with a group of international experts in the rare disease and orphan drug development field and sharing our experience. I will provide my perspective as an orphan drug developer and as a rare disease patient to facilitate the goal of the Task Force. I trust the collective efforts of the Task Force will benefit the rare disease patient community.” Richard Yang commented.
About the International Rare Diseases Research Consortium (IRDiRC): IRDiRC unites national and international governmental and non-profit funding bodies, companies (including pharmaceutical and biotech enterprises), umbrella patient advocacy organizations, and scientific researchers to promote international collaboration and advance rare diseases research worldwide. Importantly, the coverage of the Consortium is global and involves stakeholders from Africa, Asia, Australia, North America, and Europe.
For more information about IRDiRC’s “Orphan Drug Development Guidebook” Task Force,
please visit http://www.irdirc.org/activities/task-forces/orphan-drug-development-guidebook-task-force/
HONG KONG & NEW YORK–(BUSINESS WIRE)–Reflection Biotechnologies Limited (“ReflectionBio”), a gene therapy company committed to the research and development of life-changing treatments for rare diseases, today announced that the U.S.
HONG KONG & NEW YORK–(BUSINESS WIRE)–Reflection Biotechnologies Limited (“ReflectionBio”), a gene therapy company committed to the research and development of life-changing treatments for rare diseases, today announced that the U.S.
